3rd Edition of International Precision Medicine Conference

April 24-26, 2023

April 24 -26, 2023 | Orlando, Florida, USA

Rare Diseases/Disorders and Orphan Drugs

Rare Diseases/Disorders and Orphan Drugs

A disease or condition is considered rare if it affects fewer than one in every 2,000 people in the general population. There are currently about 6,000 known rare diseases, and new ones are being discovered on a regular basis in scientific literature. Word ‘Orphan’ is derived from the Greek term ‘orphanos’, which refers to a child who has lost one or both parents, as well as an adult who has lost a child. Orphan drugs are medications used to diagnose, prevent, or cure rare diseases that are life-threatening or disabling. They're called "orphans" because the pharmaceutical business has little interest in developing and marketing medications for a small proportion of patients with extremely rare diseases under normal market conditions.

  • FDA approved drugs
  • Efficacy of orphan drugs
Committee Members
Speaker at Precision Medicine Conference 2023 - Salah S Massoud

Salah S Massoud

University of Louisiana, United States
Speaker at Precision Medicine Conference 2023 - Ewa Danuta Bialek

Ewa Danuta Bialek

Institute of Psychosynthesis, Poland
Speaker at Precision Medicine Conference 2023 - Ingrid Vasiliu Feltes

Ingrid Vasiliu Feltes

MEDNAX, United States
2023 Speakers Speakers
Speaker at Precision Medicine Conference 2023 - Loubna Safar

Loubna Safar

Damascus University, Syrian Arab Republic
Speaker at Precision Medicine Conference 2023 - Abigarl Ndudzo

Abigarl Ndudzo

Lupane State University, Zimbabwe
Speaker at Precision Medicine Conference 2023 - Barbara Maria Frigieri

Barbara Maria Frigieri

Sao Paulo State University (UNESP), Brazil
Speaker at Precision Medicine Conference 2023 - Paidamoyo Kachambwa

Paidamoyo Kachambwa

Mediclinic Precise, South Africa

Submit your abstract Today

Watsapp